Gene Therapy

Improving the on-target activity of high-fidelity Cas9 editors by combining rational design and random mutagenesis

2 days ago | Springer

Abstract Genomic and post-genomic editors based on CRISPR/Cas systems are widely used in basic research and applied sciences, including human gene therapy. Most genome editing...
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RG6501 Phase 1/2a Clinical Results to Be Presented at 2023 Retinal Cell and Gene Therapy Innovation Summit

4 days ago | San Diego Biotechnology

CARLSBAD, Calif.--- $LCTX LineageCellTherapeutics-Lineage Cell Therapeutics, Inc. , a clinical-stage biotechnology company developing allogeneic cell therapies for unmet...
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EU approves Hemgenix, one-time gene therapy for hemophilia B

17 days ago | Gene Therapy

Posted on: 7 March 2023, The European Commission has conditionally approved Hemgenix , a one-time gene therapy to treat adults with hemophilia B. Hemgenix, originally...
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Maltese Patient Received World's First ND1-LHON Gene Therapy Injection Donated by Neurophth in China

17 days ago | San Diego Biotechnology

WUHAN, China and SAN DIEGO, March 7, 2023 /PRNewswire/ - Matthias Szabo Zarb, a Maltese college student, was diagnosed with Leber hereditary optic neuropathy caused by ND1...
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NEW?* PROGRAM MANAGER - CELL AND GENE THERAPY - PharmaScouts - La Jolla, CA

18 days ago | San Diego Biotechnology

The consortium is advancing development of these new technologies in a non-competitive environment, establishing best practices and standards for a...
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Assoc Director, QA - Gene Therapy Manufacturing - Insmed Incorporated - San Diego, CA

24 days ago | San Diego Biotechnology | 4 articles

Highly organized with a strong attention to detail, clarity, accuracy and conciseness. Perform audits, write reports and follow up on...
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Gene therapy startup Locanabio lays off staff, narrows focus on Duchenne

1 month ago | San Diego Biotechnology

Biotech startup Locanabio has laid off 30% of its workforce, portending a limited scope going forward for the gene therapy developer, backed with more than $150 million since...
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Commercialization of Gene Therapy is coming soon: Neurophth Completes Patient Enrollment for Phase III clinical trial for the gene therapy treatment of LHON

1 month ago | San Diego Biotechnology

WUHAN, China and SAN DIEGO, Feb. 21, 2023 /PRNewswire/ - Neurophth Therapeutics, Inc. announced today that the last patient has been enrolled in the Phase III clinical trial...
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FDA officials offer advice on gene therapy trials

1 month ago | Gene Therapy

Posted on: 9 February 2023, Officials from the US Food and Drug Administration's Center for Biologics Evaluation and Research Office of Tissues and Advanced Therapies asserted...
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Novel opto-fluidic drug delivery system for efficient cellular transfection

1 month ago | Journal of Nanobiotechnology

Intracellular drug delivery is at the heart of many diagnosis procedures and a key step in gene therapy. Research has been conducted to bypass cell barriers for controlled...
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World Biotechnology Congress 2019

Hilaris Conferences is going to host its premier World Biotechnology Congress 2019 during October 01-02, 2019, Valencia, Spain. Biotechnology 2019 Congress aim to create a... Read more ...

World Biotechnology Congress 2019

Hilaris Conferences is going to host its premier World Biotechnology Congress 2019 during October 01-02, 2019, Valencia, Spain. Biotechnology 2019 Congress aim to create a... Read more ...

2nd International Conference on Tissue Science and Regenerative Medicine

This conference is designed for experts in academia and industries working in the tissue science and regenerative field, this conference will examine cutting-edge research in... Read more ...

Staff Scientist, Bioinformatics and Data Science - Thermo Fisher Scientific...

Work with different types of experimental data and high throughput omics data, generated by platforms such as next-generation sequencing ... Read more ...

Senior Associate Scientist - In Vitro Global Safety Pharmacology - Pfizer...

Work independently and as part of a team to help design, execute, analyze / interpret data generated from experiments ranging... Read more ...

Improving expression and assembly of difficult-to-express heterologous...

Escherichia coli heat labile toxin B subunit is one of the most popular oral vaccine adjuvants and intestine adsorption enhancers. It is often expressed as a fusion partner... Read more ...

What are the Drivers of Chronic Infectious Disease?

A $1 million grant from the Steven & Alexandra Cohen Foundation will launch a UC San Diego-led national effort to more deeply study tissue samples from patients with conditions... Read more ...

Faster Slo-Mo?

Whether in sports moments, nature documentaries or animal behavior studies, a new technique developed by UC San Diego computer scientists could have far-reaching impact. In an... Read more ...

Carl Icahn turns up heat on Illumina, claims board got extra insurance ahead...

In a letter to shareholders, Icahn says Illumina's board sought additional directors & officers protection before embarking on a “value destructive war with powerful antitrust... Read more ...

IAmScience Dario Alavez Mercado

By Sarah Kiefer | Bond LSC With a few clicks and taps on a cellphone, the timeline of a seedling of corn is preserved forever. Dario Alavez Mercado is responsible for this... Read more ...

Ratiometric electrochemical OR gate assay for NSCLC-derived exosomes

Non-small cell lung cancer is the most common pathological type of LC and ranks as the leading cause of cancer deaths. Circulating exosomes have emerged as a valuable biomarker... Read more ...

EU MDR TRANSITION PERIOD EXTENSION EFFECTIVE FROM MARCH 20, 2023, ONWARD

What Happened? The Medical Device Regulation came into force on May 26, 2021. The transition period for CE certificates issued under the Medical Device Directive and Active... Read more ...

Sales Executive | Aspen Biosciences | San Diego, CA

Job Description At Aspen Biosciences, our mission is to help our customers succeed in bringing new medicines and diagnostics from the bench to the bedside by removing the... Read more ...