RNA

In an About-Face, FDA Approves Second Sarepta Muscular Dystrophy Drug

1 month ago   |   By Xconomy

Sarepta Therapeutics received an early holiday gift Thursday- approval of golodirsen , its second Duchenne muscular dystrophy treatment, which the FDA rejected in August. The agency had dinged the application over potential side effects, namely a risk of infections from the “ports” used to infuse the drug, and kidney problems observed in animals in which golodirsen and other RNA-based drugs like it were tested. Sarepta , at the time, said it was “very surprised” by the rejection, and that the FDA hadn't previously raised any issues about those side effects. Doug Ingram, CEO of the...
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Bio Roundup: Sarepta's Approval, Merck M&A, Drug Price Bill & More

Bio Roundup: Sarepta's Approval, Merck M&A, Drug Price Bill & More

1 month ago   |   By Xconomy

If you're keeping track, FDA drug approvals have been on a tear in the past month with several decisions coming well ahead of their targeted dates. And then there's Sarepta Therapeutics. Late Thursday, the FDA announced approval of the Cambridge, MA, biotech's drug for Duchenne muscular dystrophy in patients who have a specific mutation. The drug, golodirsen , is the same one the agency rejected four months ago due to safety concerns. Responding to a rejection and addressing FDA concerns can take up to one year but Sarepta says the issues were “ rapidly evaluated...
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World Biotechnology Congress 2019

Hilaris Conferences is going to host its premier World Biotechnology Congress 2019 during October 01-02, 2019, Valencia, Spain. Biotechnology 2019 Congress aim to create a... Read more ...

World Biotechnology Congress 2019

Hilaris Conferences is going to host its premier World Biotechnology Congress 2019 during October 01-02, 2019, Valencia, Spain. Biotechnology 2019 Congress aim to create a... Read more ...

2nd International Conference on Tissue Science and Regenerative Medicine

This conference is designed for experts in academia and industries working in the tissue science and regenerative field, this conference will examine cutting-edge research in... Read more ...

Allergan Offloads Two Drugs to Secure Approval of Merger With AbbVie

Allergan Offloads Two Drugs to Secure Approval of Merger With AbbVie

Allergan is selling off an experimental drug and a commercialized product in order to allay antitrust concerns from regulators reviewing the company's $63 billion acquisition... Read more ...

When Snakes Strike: SMRT Sequencing Reveals Hidden “Venom-ome”

When Snakes Strike: SMRT Sequencing Reveals Hidden “Venom-ome”

A team of scientists from SciGenom Research Foundation in India has assembled the genome and transcriptome of the lethal Indian Cobra using PacBio long-read sequencing Snake... Read more ...

Life Sciences IPOs Target Collective Raise of More Than $600M This Week

Life Sciences IPOs Target Collective Raise of More Than $600M This Week

So far this year four privately held companies have made the transition to trading on the public markets. By month's end, five more are anticipated to join the class of 2020... Read more ...

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Sorrento Therapeutics rejects $1 billion buyout offer

San Diego company says offer undervalues the company; updates progress on novel pain management therapies... Read more ...

Shipping and Fulfillment Clerk - Gateway Genomics - La Jolla, CA

We are a boutique and innovative biotech company with a fun, friendly and motivational atmosphere. Gateway Genomics is seeking a motivated individual to join...From Indeed... Read more ...

103598 Radiologic Technician - Per Diem

SURGERY Salary commensurate with qualifications and experienceFiling Deadline: Mon 2/10/2020... Read more ...

Getting to the root of plant survival

When facing a volatile climate, nature searches for a way to survive. For plants, that often means spreading new roots deeper and wider in search of water, particularly in... Read more ...

Genetic marking discovery improves fruit quality, bolsters climate defenses

Transferring genetic markers in plant breeding is a challenge, but a team of grapevine breeders and scientists at Cornell University have come up with a powerful new method... Read more ...

Wild tomatoes resist devastating bacterial canker

Many New York tomato growers are familiar with the scourge of bacterial canker-the wilted leaves and blistered fruit that can spoil an entire season's planting. For those whose... Read more ...